Duchenne muscular dystrophy (DMD)

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Biotech

FDA rejects Capricor’s DMD cell therapy, asks for more data

The rejection raises questions about whether the new-look FDA leadership may be rowing back from some of the flexibility shown by the old regime.
Nick Paul Taylor Jul 11, 2025 9:18am
Goal disorientation and lack of vision

UPDATED: Taiho’s discontinues ph. 3 trial after DMD miss

Jul 8, 2025 10:17am
FDA
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FDA investigates 2 deaths after Sarepta Duchenne gene therapy

Jun 25, 2025 10:26am
Redbrick building with Sarepta name and logo
Favicon Fierce Pharma

2nd patient dies after Sarepta's DMD gene therapy Elevidys

Jun 16, 2025 10:58am
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RegenXBio links DMD gene therapy to improved outcomes

Jun 5, 2025 8:52am
Layoffs

Keros culls phase 2 PAH program, 70 staff roles

May 29, 2025 10:10am