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Metabolic disorders
Research
Boy with rare disease 'thriving' after 1st custom gene therapy
Born with a serious metabolic disease, scientists raced to prepare a custom CRISPR gene editing therapy for KJ in just six months.
Darren Incorvaia
May 15, 2025 1:00pm
Relmada reconsiders plans to test psilocybin for obesity
Mar 28, 2025 10:00am
Novo bets up to $354M per target on Gensaic’s delivery tech
Mar 3, 2025 8:37am
Lilly inks $50M deal for biotech's FXR program
Feb 26, 2025 5:35am
Novo inks $50M metabolic disease pact with genomics biotech
Jan 7, 2025 10:35am
Advantage spins out anti-aging R&D to new biotech Klothea
Nov 25, 2024 11:56am