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Metabolic disorders

Gene editing therapy patient KJ with Drs Ahrens-Nicklas and Musunuru
Research

Boy with rare disease 'thriving' after 1st custom gene therapy

Born with a serious metabolic disease, scientists raced to prepare a custom CRISPR gene editing therapy for KJ in just six months.
Darren Incorvaia May 15, 2025 1:00pm
magic mushroom

Relmada reconsiders plans to test psilocybin for obesity

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Novo bets up to $354M per target on Gensaic’s delivery tech

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gold arrow pointing upward forward

Lilly inks $50M deal for biotech's FXR program

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the world and DNA or genes

Novo inks $50M metabolic disease pact with genomics biotech

Jan 7, 2025 10:35am
red wheel of fortune

Advantage spins out anti-aging R&D to new biotech Klothea

Nov 25, 2024 11:56am

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