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Niemann-Pick type C disease
Biotech
Azafaros' €132M series B will fund brain-penetrant drug trials
Azafaros has secured 132 million euros in series B funds that the Dutch biotech will use to push its brain disease drug through two late-stage trials.
James Waldron
May 13, 2025 7:10am
Cyclo Therapeutics merges with longtime backer Rafael Holdings
Aug 22, 2024 8:50am
'Clinical intuition' led FDA advisors to back Zevra's rare disease med
Aug 5, 2024 10:35am
Orphazyme meme ends with $13M sale to satisfy bankruptcy court
May 16, 2022 6:06am
Roche-partnered Scenic nabs $31M to test 3 rare disease meds
Mar 10, 2022 10:12am
Orphazyme to assess strategic options after EU advisers nix drug
Feb 24, 2022 10:45am