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Niemann-Pick type C disease

Brain wrapped in cash money
Biotech

Azafaros' €132M series B will fund brain-penetrant drug trials

Azafaros has secured 132 million euros in series B funds that the Dutch biotech will use to push its brain disease drug through two late-stage trials.
James Waldron May 13, 2025 7:10am
MA strategy deal block push come together form

Cyclo Therapeutics merges with longtime backer Rafael Holdings

Aug 22, 2024 8:50am
accelerated

'Clinical intuition' led FDA advisors to back Zevra's rare disease med

Aug 5, 2024 10:35am
signing contract

Orphazyme meme ends with $13M sale to satisfy bankruptcy court

May 16, 2022 6:06am
Amsterdam canal

Roche-partnered Scenic nabs $31M to test 3 rare disease meds

Mar 10, 2022 10:12am
Lots of nos

Orphazyme to assess strategic options after EU advisers nix drug

Feb 24, 2022 10:45am

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